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| ID | Phase | Actuator | Vector | Target Cells | Sponsor | Condition | Results |
| NCT03326336 (PIONEER) | I/IIa | ChrimsonR | AAV 2.7m8 | RGC | GenSight Biologic | RP | Case report: Object localization in near spase, EEG ( Sahel et al., 2021) |
| NCT04945772 (RESTORE), NCT06162585 | I/II + Und Follow-Up Studie | MCO-010 | AAV2 | BC | Nanoscope Therapeutics | RP | Press release: Significant improvement in VA ( FirstWord, 2025; Nanoscope Therapeutics, 2024 ) |
| NCT04919473, NCT05921162 | I/II + Und Follow-Up Studie | MCO-1 / vMCO-010 | AAV2 | BC | Nanoscope Therapeutics | RP, ABCA4-associated | Case Series: Improvement in VA, visual field and Quality of Life, no controls included (Mohanty et al., 2025 ) |
| NCT05417126 (STARLIGHT), NCT06048185 | II + Und Follow-Up Studie | vMCO-010 | AAV2 | BC | Nanoscope Therapeutics | M. Stargardt | Case Series: Improvement in VA, visual field and Quality of Life, no controls included (Lam et al., 2025) |
| NCT02556736 | I/IIa | ChR2 | AAV2.7m8 | RGC | AbbVie/RetroSense | RP | Conference report (Bunnell, Yuan, Lopez, 2025) |
| NCT04278131 | I/II | ChronosFP | AAV2 | RGC | Bionic Sight | RP | Press release: Increase in light sensitivity and VA ( Bionic Sight, 2025 ) |
| NCT06460844 (ENVISION) | I | ChRown | ARMMs | RGC | Ray Therapeutics | RP, Choroideremia | Sponsor's webpage ( Ray Therapeutics, 2025) |
| NCT06292650 | I | PsCatCh2.0 | AAV? | RGC | Zhongmou Therapeutics | RP | Conference report: VA improvement (Zhou et al., 2025) |
| ChiCTR2200062174 | ? | ? | AAV? | ? | Ugenex Therapeutics | PR | Conference report: VA improvement (Luo et al., 2025) |